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The WFH Guidelines for the Management of Haemophilia: AAV Gene Therapy, 2025

  • Glenn F. Pierce
  • , Margareth C. Ozelo
  • , Johnny Mahlangu
  • , Amy L. Dunn
  • , Marlene Beijlevelt
  • , Rose Bender
  • , Manuel Carcao
  • , Donna Coffin
  • , Enrico Ferri Grazzi
  • , Graham R. Foster
  • , Julie Frantsve-Hawley
  • , Alfonso Iorio
  • , Shannon Jackson
  • , Radoslaw Kaczmarek
  • , Gwendolyn E. Kaeser
  • , Barbara A. Konkle
  • , Magdalena Lewandowska
  • , Wolfgang Miesbach
  • , Brian O'Mahony
  • , Steven Pipe
  • Ulrike M. Reiss, Amy K. Wilson, Emna Gouider, Miguel Escobar, the WFH AAV Gene Therapy Guidelines Expert Panel
  • World Federation of Hemophilia
  • Universidade Estadual de Campinas
  • University of the Witwatersrand
  • Ohio State University
  • Amsterdam UMC - University of Amsterdam
  • Yale University
  • University of Toronto
  • Federation of Haemophilia Associations (FedEmo)
  • Queen Mary University of London
  • EBQ Consulting
  • McMaster University
  • Providence Health Care Canada
  • Indiana University Bloomington
  • LLC
  • University of Washington
  • Indiana Hemophilia and Thrombosis Center
  • Goethe University Frankfurt
  • Irish Haemophilia Society
  • University of Michigan, Ann Arbor
  • St. Jude Children Research Hospital
  • Children's Minnesota Center for Bleeding and Clotting Disorders
  • Université de Tunis El Manar
  • University of Texas Health Science Center at Houston

Research output: Contribution to journalArticleAcademicpeer-review

19 Downloads (Pure)
Original languageEnglish
JournalHaemophilia
Early online date2025
DOIs
Publication statusE-pub ahead of print - 2025
Externally publishedYes

Keywords

  • AAV gene therapy
  • bleeding disorders
  • haemophilia
  • management guidelines
  • monitoring
  • outcomes
  • shared decision-making

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