Skip to main navigation Skip to search Skip to main content

Lentiviral Stem Cell Gene Therapy for Pompe Disease

  • Qiushi Liang
  • , Merel Stok
  • , Yvette van Helsdingen
  • , Guus van der Velden
  • , Ed Jacobs
  • , Dirk Duncker
  • , Arnold Reuser
  • , Ans van der Ploeg
  • , Arnold Vulto
  • , Niek P van Til
  • , Gerard Wagemaker

Research output: Contribution to journalArticleAcademicpeer-review

Original languageEnglish
Pages (from-to)S64
JournalJournal of neuromuscular diseases
Volume2
Issue numbers1
Publication statusPublished - 2015

Cite this