Projects per year
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Dive into the research topics where Niek van Til is active. These topic labels come from the works of this person. Together they form a unique fingerprint.
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Projects
- 8 Active
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Gene Therapy for VWM: ADENO-ASSOCIATED VIRUS VECTOR GENE THERAPY FOR VANISHING WHITE MATTER
van der Knaap, M. (Principal investigator) & van Til, N. (Project Leader)
01/04/2025 → 31/03/2029
Project: Research
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WAR 2024-20: Human brains in a dish to test AAV gene therapy for vanishing white matter
van der Knaap, M. (Principal investigator) & van Til, N. (Project Leader)
01/08/2024 → 30/04/2026
Project: Research
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PP 32780 Gene therapy for VWM: PP 32780 Gene therapy for Vanishing White Matter
van Til, N. (Project Leader)
15/08/2023 → 31/08/2025
Project: Research
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Gene therapy for VWM: Gene therapy for Vanishing White Matter
van der Knaap, M. (Principal investigator) & van Til, N. (Project Leader)
15/08/2023 → 31/08/2025
Project: Research
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VWM mechanisme en medicament8a: VWM mechanisme en medicamenten, Klene project 8a
van der Knaap, M. (Principal investigator) & van Til, N. (Project Leader)
01/01/2022 → 31/12/2026
Project: Research
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Assessment of non-myelotoxic agents as a preparatory regimen for hematopoietic stem cell gene therapy
Şeker, M. E., Erol, Ö. D., Pervin, B., Wagemaker, G., van Til, N. P. & Aerts-Kaya, F., 1 Jan 2025, In: Human Cell. 38, 1, 9.Research output: Contribution to journal › Article › Academic › peer-review
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Draining the brain: Gene therapy reverses brain edema in mice with the leukodystrophy MLC
Min, R., van Til, N. P. & van der Knaap, M. S., 7 May 2025, In: Molecular therapy. 33, 5, p. 1872-1873 2 p.Research output: Contribution to journal › Comment/Letter to the editor › Academic
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Advanced Therapy Medicinal Products: Clinical, Non-clinical, and Quality Considerations
Mastrobattista, E., Doevendans, E., van Til, N. P., Kemp, V., de Vrij, J. & Hoogendoorn, K., 1 Jan 2024, Pharmaceutical Biotechnology: Fundamentals and Applications, Sixth Edition. Springer International Publishing, p. 323-399 (Pharmaceutical Biotechnology: Fundamentals and Applications, Sixth Edition).Research output: Chapter in Book/Report/Conference proceeding › Chapter › Academic › peer-review
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Correction of Griscelli Syndrome Type 2 causing mutations in the RAB27A gene with CRISPR/Cas9
Erol, Ö. D., Şenocak, Ş., Özçimen, B., Güney Esken, G. L., Kiliç, H. B., Kocaefe, Ç., VAN TIL, N. P. & Aerts Kaya, F., 2024, In: Turkish Journal of Biology. 48, 5, p. 290-298 9 p.Research output: Contribution to journal › Article › Academic › peer-review
Open AccessFile1 Downloads (Pure) -
Gene Therapy for Inherited Liver Disease: To Add or to Edit
Chen, Y., van Til, N. P. & Bosma, P. J., 1 Dec 2024, In: International journal of molecular sciences. 25, 23, 12514.Research output: Contribution to journal › Review article › Academic › peer-review
Open AccessFile1 Citation (Scopus)1 Downloads (Pure)